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RECRUITING
Updated: Mar 21, 2024

A Head-to-head Study Comparing the Functional Value of Two Models of Robotically Assisted Rehabilitation in SMA (Spinal Muscular Atrophy) Patients (SMArt)

Phase
N/A
Early 1
1
2
3
4

Brief Summary

A head-to-head study comparing the functional value of two models of robotically assisted rehabilitation in patients with SMA. A single-center, randomized, single-blinded, comparative study of Robotically Assisted Verticalization versus Robotically Assisted Locomotion.

The objective of research:

The main goal of the project is to determine the optimal robotically assisted rehabilitation model for people with SMA depending on age and baseline functional status. The study consists of a head-to-head comparison of two rehabilitation models.

  1. Research period: 4 years
  2. Patients age: 0-21 y.o.
  3. Group size: 200 patients (100 patients in each group)
  4. Assignment of patients to study groups in a randomised manner

Key Information

Inclusion Criteria:

  • Signing of informed consent to participate in the experiment by the participant or the participant's parent/legal guardian
  • Diagnosis of SMA (spinal muscular atrophy 1-4) confirmed by genetic testing, symptomatic or pre-symptomatic
  • Age between 0 and 21 years of age (will be determined on the day of starting participation in the project based on the date of birth)
  • Treatment under a drug program for spinal muscular atrophy, provided that the patient has a diagnosis of spinal muscular atrophy at the date of eligibility.

Exclusion Criteria:

  • Cardio-respiratory disorders requiring invasive ventilation
  • Advanced osteoporosis with multiple fractures prior to treatment
  • Functional deterioration during the rehabilitation process in the range of scales appropriately selected for the SMA type: Prechtl, HINE, CHOP-INTEND, HFMS, RULM
  • Lack of cooperation with the therapist
  • Other functional indications preventing exercise

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